Targeted approaches to induce immune tolerance for Pompe disease therapy: Molecular Therapy - Methods & Clinical Development
Pompe Disease | ASGCT - American Society of Gene & Cell Therapy
Pompe disease treatment: What are the options? | Pompe Disease News
Biomedicines | Free Full-Text | Gene Therapy Developments for Pompe Disease
Advancing the Treatment of Pompe Disease: Clinical Updates in Newborn Screening and Enzyme Replacement | PPT
Enzyme Replacement Therapy Can Reverse Pathogenic Cascade in Pompe Disease - ScienceDirect
Frontiers | Recommendations for Infantile-Onset and Late-Onset Pompe Disease: An Iranian Consensus
Pompe Disease - Physiopedia
Pompeandyou.com | About Pompe disease
Rescue of Advanced Pompe Disease in Mice with Hepatic Expression of Secretable Acid α-Glucosidase - ScienceDirect
Pompe Disease Therapeutic Market Share Expected to Grow at a CAGR of 3.5% by 2027 | Growing Demand Drives the market in Healthcare | Medgadget
Progress and challenges of gene therapy for Pompe disease. | Semantic Scholar
Pompe Disease – newbornscreening.info
Biomolecules | Free Full-Text | Pompe Disease: New Developments in an Old Lysosomal Storage Disorder
Pompe Disease (also called Glycogen storage disease type 2) | CheckRare
Gene therapy for the treatment of Pompe disease. The therapeutic gene... | Download Scientific Diagram
Diagnosis and treatment of late-onset Pompe disease in the Middle East and North Africa region: consensus recommendations from an expert group | BMC Neurology | Full Text
About Pompe Disease - SaveChloe
Muscle‐directed gene therapy corrects Pompe disease and uncovers species‐specific GAA immunogenicity | EMBO Molecular Medicine
