Long-Term Prognosis of Patients with Infantile-Onset Pompe Disease Diagnosed by Newborn Screening and Treated since Birth
A Systematic Review of the Health Economics of Pompe Disease | PharmacoEconomics - Open
Pompe Disease: Long-Term Follow-up Clinical Guidelines
A Systematic Review of the Health Economics of Pompe Disease | PharmacoEconomics - Open
The effectiveness of enzyme replacement therapy for juvenile‐onset Pompe disease: A systematic review - Milverton - 2019 - Journal of Inherited Metabolic Disease - Wiley Online Library
Enzymatic diagnosis of Pompe disease: lessons from 28 years of experience | European Journal of Human Genetics
Pompe disease: pathogenesis, molecular genetics and diagnosis | Aging
Pompe Disease – AVROBIO
NICE recommend new treatment option for late-onset Pompe disease | Muscular Dystrophy UK
Pompe Disease – newbornscreening.info
Survival and associated factors in 268 adults with Pompe disease prior to treatment with enzyme replacement therapy | Orphanet Journal of Rare Diseases | Full Text
How Does Pompe Disease Affect Life Expectancy? | Pompe Disease News
Pompeandyou.com | About Pompe disease
Pompe 6neo Mouse Model - QPS Neuropharmacology
Early Treatment With Alglucosidase Alfa Prolongs Long-Term Survival of Infants With Pompe Disease | Pediatric Research
Pompe Disease| Symptoms Causes Diagnosis Treatment | Onlymyhealth
Survival and associated factors in 268 adults with Pompe disease prior to treatment with enzyme replacement therapy | Orphanet Journal of Rare Diseases | Full Text
Survival and associated factors in 268 adults with Pompe disease prior to treatment with enzyme replacement therapy | Orphanet Journal of Rare Diseases | Full Text
Pompe Disease: Early Diagnosis and Early Treatment Make a Difference - ScienceDirect
Cost related to Pompe disease treatment | Download Table
Pompe Disease Therapeutic Pipeline Landscape Constituting Novel Drugs
